Exon7 Targeted CRISPR-Prime Editing Approaches for SMN2 Gene Editing in Spinal Muscular Atrophy (SMA) Disease Can Increase In Vitro SMN Expression

BAL E., Yelgen G., Odabaş S. P., Metin A. S., Karakaya E., Gülden G., ...More

Cold Spring Harbor Laboratory, 2022 (Peer-Reviewed Journal)

• Publication Type: Article / Article
• Publication Date: 2022
• Doi Number: 10.1101/2022.03.21.484406
• Journal Name: Cold Spring Harbor Laboratory
• Istanbul Kültür University Affiliated: No